ATC Group: A16AX06 Miglustat

Anatomical Therapeutic Chemical Classification System

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Miglustat

Hierarchical Position

Active Ingredients

Chemical substance
Description

Miglustat is an inhibitor of glucosylceramide synthase, the enzyme responsible for the first step in the synthesis of most glycolipids. Miglustat is indicated for the treatment of adult patients with mild to moderate type 1 Gaucher disease and for the treatment of progressive neurological manifestations in patients with Niemann-Pick type C disease.